B Thalassemia

Also known as: Β -Thalassemia / Β Thalassemia / Thalassemia, Beta / B-Thalassemia / Β-thalassemia / Thalassaemia beta / Beta Thalassaemia / Beta Thalassemia / Beta-Thalassemia / Thalassemia beta / Beta thalassemia (disorder) / Beta-thalassaemia / Thalassaemia intermedia / Thalassemia intermedia (disorder) / Thalassemia intermedia / Mediterranean anemia / Mediterranean anaemia / Thalassemia major / Cooley's anaemia / Thalassaemia major / Thalassemia major (disorder) / Homozygous beta thalassemia (disorder) / Cooley's anemia

DrugDrug NameDrug Description
DB16900Betibeglogene autotemcelA hematopoietic stem cell-based gene therapy used in the treatment of β-thalassemia in adult and pediatric patients who require regular red blood cell transfusions.
DB12281LuspaterceptAn erythroid maturation agent used to treat anemia secondary to beta thalassemia, myelodysplastic syndromes, and neoplasms.
DrugDrug NameTargetType
DB16900Betibeglogene autotemcelAlpha globintarget
DrugDrug NamePhaseStatusCount
DB01609Deferasirox1Completed1
DB13120Deferitazole1Completed1
DB16069SP-4201Terminated1
DB177062,2-Dimethylbutyrate1 / 2Completed1
DB00087Alemtuzumab1 / 2Recruiting1
DB18136Briquilimab1 / 2Recruiting1
DB16132Deferitrin1 / 2Completed1
DB00099Filgrastim1 / 2Recruiting1
DB01005Hydroxyurea1 / 2Recruiting1
DB06809Plerixafor1 / 2Recruiting1
DB00877Sirolimus1 / 2Recruiting1
DB00087Alemtuzumab2Active Not Recruiting1
DB00087Alemtuzumab2Completed1
DB09312Antilymphocyte immunoglobulin (horse)2Completed1
DB00098Antithymocyte immunoglobulin (rabbit)2Recruiting1
DB00125Arginine2Completed1
DB00928Azacitidine2Completed1
DB11105Benzalkonium2Recruiting1
DB12426Bitopertin2Completed1
DB00188Bortezomib2Recruiting1
DB01008Busulfan2Active Not Recruiting1
DB01008Busulfan2Completed2
DB00531Cyclophosphamide2Completed2
DB00531Cyclophosphamide2Recruiting1
DB00091Cyclosporine2Completed1
DB01609Deferasirox2Completed2
DB01609Deferasirox2Withdrawn1
DB08826Deferiprone2Terminated1
DB13120Deferitazole2Completed1
DB13120Deferitazole2Terminated1
DB13120Deferitazole2Withdrawn1
DB00746Deferoxamine2Completed1
DB00746Deferoxamine2Terminated1
DB01234Dexamethasone2Recruiting1
DB00016Erythropoietin2Completed1
DB01073Fludarabine2Active Not Recruiting1
DB01073Fludarabine2Completed1
DB01073Fludarabine2Recruiting1
DB01005Hydroxyurea2Completed2
DB01005Hydroxyurea2Unknown Status1
DB12281Luspatercept2Completed2
DB12281Luspatercept2Recruiting2
DB01042Melphalan2Completed1
DB00688Mycophenolate mofetil2Completed1
DB00688Mycophenolate mofetil2Recruiting1
DB00073Rituximab2Recruiting1
DB17724Rusfertide2Completed2
DB16069SP-4202Withdrawn1
DB00877Sirolimus2Completed1
DB00877Sirolimus2Recruiting1
DB00864Tacrolimus2Recruiting1
DB01041Thalidomide2Completed1
DB04572Thiotepa2Completed1
DB16193Tovinontrine2Terminated1
DB17692Vamifeport2Completed1
DB17692Vamifeport2Withdrawn1
DB15572Exagamglogene autotemcel2 / 3Active Not Recruiting1
DB01005Hydroxyurea2 / 3Completed2
DB00264Metoprolol2 / 3Completed1
DB06206Sugammadex2 / 3Unknown Status1
DB01041Thalidomide2 / 3Completed2
DB00399Zoledronic acid2 / 3Unknown Status1
DB01609Deferasirox3Completed2
DB00746Deferoxamine3Completed1
DB15572Exagamglogene autotemcel3Enrolling by Invitation1
DB15572Exagamglogene autotemcel3Recruiting2
DB12281Luspatercept3Completed1
DB12281Luspatercept3Recruiting1
DB01609Deferasirox4Completed1
DB08826Deferiprone4Completed1
DB08826Deferiprone4Unknown Status1
DB00746Deferoxamine4Completed1
DB09027Ledipasvir4Completed1
DB08934Sofosbuvir4Completed1
DB00381AmlodipineNot AvailableUnknown Status1
DB00125ArginineNot AvailableCompleted1
DB01262DecitabineNot AvailableCompleted1
DB01609DeferasiroxNot AvailableUnknown Status1
DB08826DeferiproneNot AvailableCompleted1
DB08826DeferiproneNot AvailableUnknown Status1
DB00746DeferoxamineNot AvailableCompleted1
DB00746DeferoxamineNot AvailableUnknown Status1
DB00099FilgrastimNot AvailableCompleted1
DB01005HydroxyureaNot AvailableCompleted1
DB12281LuspaterceptNot AvailableRecruiting1
DB06809PlerixaforNot AvailableCompleted1
DB00203SildenafilNot AvailableCompleted1