Severe Haemophilia A
Also known as: Hemophilia A, Severe / Severe Hemophilia A / Severe hemophilia A (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB15561 | Valoctocogene roxaparvovec | An adeno-associated virus serotype 5 (AAV5)-based gene therapy containing a coagulation factor VIII complementary DNA used to treat severe hemophilia A. |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB15561 | Valoctocogene roxaparvovec | Coagulation factor VIII (F8) | target |