Amyloidosis, Hereditary

Also known as: Hereditary Amyloidosis / Hereditary amyloidosis (disorder) / Familial amyloidosis / Amyloidosis, Familial / Neuropathic heredofamilial amyloidosis / Hereditary neuropathic amyloidosis / Amyloid Neuropathies, Familial / Familial amyloid polyneuropathy / Familial amyloid polyneuropathy (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB14582Patisiran3Active Not Recruiting1
DB14582Patisiran3Completed1
DB16309Revusiran3Completed1
DB16699Vutrisiran3Active Not Recruiting1
DB14713InotersenNot AvailableApproved for Marketing1
DB14582PatisiranNot AvailableNo Longer Available1