Neurofibromatosis Type 1 (NF1)

Also known as: NF 1 / Neurofibromatosis, type 1 (von Recklinghausen's disease) / NF1 / Neurofibromatosis 1 (NF1) / Neurofibromatosis Type 1 / Neurofibromatosis Type I / Von Recklinghausen Disease / Neurofibromatosis 1 / Neurofibromatosis I / Neurofibromatosis, type 1 / Neurofibromatosis type 1 (disorder) / Von Recklinghausen's disease (of nerve) / Neurofibromatosis, unspecified / Neurofibromatoses / Neurofibromatosis / Neurofibromatosis (morphologic abnormality) / Neurofibromatosis syndrome (disorder)

DrugDrug NameDrug Description
DB11689SelumetinibA MEK 1/2 inhibitor used in pediatric patients to treat neurofibromatosis type 1 (NF1) accompanied by symptomatic, inoperable plexiform neurofibromas (PN).
DrugDrug NamePhaseStatusCount
DB04868Nilotinib0Completed1
DB01270Ranibizumab0Completed1
DB15254Avutometinib1Recruiting1
DB00958Carboplatin1Completed1
DB03619Deoxycholic acid1Not Yet Recruiting1
DB03619Deoxycholic acid1Recruiting2
DB00724Imiquimod1Completed1
DB00227Lovastatin1Completed1
DB10315Measles virus vaccine live attenuated1Recruiting1
DB04951Pirfenidone1Completed1
DB06811Polidocanol1Not Yet Recruiting1
DB06811Polidocanol1Recruiting2
DB08910Pomalidomide1Completed1
DB11689Selumetinib1Active Not Recruiting1
DB11689Selumetinib1Completed2
DB11119Sodium iodide1Recruiting1
DB00398Sorafenib1Completed1
DB00570Vinblastine1Completed1
DB12001Abemaciclib1 / 2Recruiting1
DB00928Azacitidine1 / 2Not Yet Recruiting1
DB00987Cytarabine1 / 2Not Yet Recruiting1
DB01073Fludarabine1 / 2Not Yet Recruiting1
DB07101Mirdametinib1 / 2Recruiting1
DB11689Selumetinib1 / 2Active Not Recruiting1
DB11689Selumetinib1 / 2Recruiting2
DB08911Trametinib1 / 2Not Yet Recruiting1
DB06151Acetylcysteine2Active Not Recruiting1
DB06151Acetylcysteine2Recruiting1
DB00855Aminolevulinic acid2Recruiting1
DB00112Bevacizumab2Completed1
DB11967Binimetinib2Active Not Recruiting1
DB01008Busulfan2Recruiting1
DB05153Cabozantinib2Completed1
DB08875Cabozantinib2Completed1
DB04849Cediranib2Terminated1
DB00482Celecoxib2Completed1
DB00169Cholecalciferol2Terminated1
DB00151Cysteine2Active Not Recruiting1
DB00151Cysteine2Recruiting1
DB00586Diclofenac2Completed1
DB00997Doxorubicin2Completed1
DB11714Durvalumab2Not Yet Recruiting1
DB00773Etoposide2Completed1
DB01590Everolimus2Completed2
DB00099Filgrastim2Completed1
DB01073Fludarabine2Recruiting1
DB17293Hiltonol2Recruiting1
DB15127Hydrogen2Completed1
DB01181Ifosfamide2Completed1
DB05258Interferon alfa2Completed1
DB00480Lenalidomide2Completed1
DB01202Levetiracetam2Recruiting1
DB00227Lovastatin2Completed1
DB00227Lovastatin2Recruiting1
DB01042Melphalan2Recruiting1
DB00563Methotrexate2Completed1
DB07101Mirdametinib2Active Not Recruiting1
DB00471Montelukast2Active Not Recruiting1
DB00471Montelukast2Recruiting1
DB18102Nedometinib2Completed2
DB04951Pirfenidone2Completed1
DB00073Rituximab2Recruiting1
DB11689Selumetinib2Active Not Recruiting1
DB11689Selumetinib2Completed2
DB11689Selumetinib2Not Yet Recruiting3
DB11689Selumetinib2Recruiting1
DB11689Selumetinib2Withdrawn2
DB00877Sirolimus2Completed2
DB00398Sorafenib2Terminated1
DB14546Sulfate ion2Completed1
DB14546Sulfate ion2Withdrawn1
DB01268Sunitinib2Terminated1
DB00853Temozolomide2Completed1
DB04960Tipifarnib2Completed1
DB08911Trametinib2Active Not Recruiting2
DB00570Vinblastine2Completed1
DB00541Vincristine2Completed1
DB11094Vitamin D2Terminated1
DB00555Lamotrigine2 / 3Terminated1
DB00958Carboplatin3Recruiting1
DB15127Hydrogen3Recruiting1
DB11689Selumetinib3Active Not Recruiting1
DB11689Selumetinib3Recruiting1
DB14546Sulfate ion3Recruiting1
DB00541Vincristine3Recruiting1
DB08912Dabrafenib4Recruiting1
DB00422Methylphenidate4Completed1
DB08911Trametinib4Recruiting1
DB12091GadoliniumNot AvailableTerminated1
DB00227LovastatinNot AvailableCompleted1