Beta-Thalassemia Major

Also known as: Beta Thalassemia Major Anemia / Anemia, Cooley's / Beta Thalassemia Major / Β-thalassemia Major / Β Thalassemia Major / Cooley's anemia / Beta thalassemia / Mediterranean anemia / Mediterranean anaemia / Thalassemia major / Cooley's anaemia / Thalassaemia major / Thalassemia major (disorder) / Homozygous beta thalassemia (disorder) / Thalassemia beta / Beta thalassaemia / Beta thalassemia (disorder) / Thalassaemia beta / Beta-thalassaemia / Beta-Thalassemia

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00098Antithymocyte immunoglobulin (rabbit)0Withdrawn1
DB00188Bortezomib0Withdrawn1
DB16741Bortezomib D-mannitol0Withdrawn1
DB01008Busulfan0Withdrawn1
DB00531Cyclophosphamide0Withdrawn1
DB01234Dexamethasone0Withdrawn1
DB01073Fludarabine0Withdrawn1
DB00688Mycophenolate mofetil0Withdrawn1
DB00073Rituximab0Withdrawn1
DB00864Tacrolimus0Withdrawn1
DB00087Alemtuzumab1 / 2Completed1
DB00087Alemtuzumab1 / 2Recruiting1
DB16900Betibeglogene autotemcel1 / 2Completed1
DB00091Cyclosporine1 / 2Completed1
DB01073Fludarabine1 / 2Completed1
DB01073Fludarabine1 / 2Recruiting1
DB01005Hydroxyurea1 / 2Recruiting1
DB01042Melphalan1 / 2Completed1
DB00688Mycophenolate mofetil1 / 2Completed1
DB00073Rituximab1 / 2Recruiting1
DB00864Tacrolimus1 / 2Completed1
DB04572Thiotepa1 / 2Recruiting1
DB01609Deferasirox2Completed1
DB12192Emeramide2Completed1
DB16069SP-4202Recruiting1
DB12118Sotatercept2Terminated1
DB01609Deferasirox2 / 3Unknown Status1
DB08826Deferiprone2 / 3Unknown Status2
DB00746Deferoxamine2 / 3Unknown Status1
DB09298Silibinin2 / 3Unknown Status1
DB06643Denosumab3Terminated1
DB09027Ledipasvir3Recruiting1
DB08934Sofosbuvir3Recruiting1
DB00399Zoledronic acid3Terminated1
DB00074Basiliximab4Unknown Status1
DB00091Cyclosporine4Unknown Status1
DB01609Deferasirox4Completed1
DB01609Deferasirox4Withdrawn1
DB08826Deferiprone4Completed1
DB00331Metformin4Unknown Status1
DB00563Methotrexate4Unknown Status1
DB00688Mycophenolate mofetil4Unknown Status1
DB00381AmlodipineNot AvailableCompleted1
DB00125ArginineNot AvailableCompleted1
DB01262DecitabineNot AvailableCompleted1
DB01609DeferasiroxNot AvailableCompleted1
DB08826DeferiproneNot AvailableCompleted2
DB00746DeferoxamineNot AvailableCompleted1
DB14865Human interleukin-2Not AvailableUnknown Status1
DB00203SildenafilNot AvailableCompleted1
DB14744Spirulina platensisNot AvailableCompleted1
DB00163Vitamin ENot AvailableCompleted1