PIK3CA-Related Overgrowth Spectrum (PROS)

Also known as: PIK3CA-related Overgrowth Spectrum / PIK3CA Related Overgrowth Spectrum / Phosphatidylinositol-4,5-bisphosphate 3-kinase catalytic subunit alpha related overgrowth syndrome (disorder)

DrugDrug NameDrug Description
DB12015AlpelisibAlpelisib is indicated in combination with fulvestrant to treat postmenopausal women, and men, with advanced or metastatic breast cancer. This cancer must be hormone receptor (HR)-positive, human epidermal growth factor...
DrugDrug NamePhaseStatusCount
DB12015Alpelisib2Active Not Recruiting1
DB12015Alpelisib2Not Yet Recruiting1
DB12015Alpelisib2Recruiting1
DB07101Mirdametinib2Not Yet Recruiting1
DB14954PIK3CA2Completed1
DB00877Sirolimus2Completed1
DB12015AlpelisibNot AvailableAvailable1
DB14982MiransertibNot AvailableNo Longer Available1