Leber Congenital Amaurosis (LCA)
Also known as: Leber Congenital Amaurosis / Leber's congenital amaurosis / LCA (Leber Congenital Amaurosis) / Leber's amaurosis (disorder)
| Drug | Drug Name | Drug Description |
|---|
| Drug | Drug Name | Target | Type |
|---|
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB13932 | Voretigene neparvovec | 1 | Completed | 1 |
| DB12112 | Zuretinol acetate | 1 | Completed | 2 |
| DB18327 | ATSN-101 | 1 / 2 | Active Not Recruiting | 1 |
| DB18666 | HG004 | 1 / 2 | Recruiting | 1 |
| DB18277 | OCU400 | 1 / 2 | Recruiting | 1 |
| DB00781 | Polymyxin B | 1 / 2 | Active Not Recruiting | 1 |
| DB00860 | Prednisolone | 1 / 2 | Active Not Recruiting | 1 |
| DB00635 | Prednisone | 1 / 2 | Active Not Recruiting | 1 |
| DB16327 | Sepofarsen | 1 / 2 | Completed | 1 |
| DB16327 | Sepofarsen | 1 / 2 | Terminated | 1 |
| DB00440 | Trimethoprim | 1 / 2 | Active Not Recruiting | 1 |
| DB13932 | Voretigene neparvovec | 1 / 2 | Active Not Recruiting | 1 |
| DB16327 | Sepofarsen | 2 / 3 | Active Not Recruiting | 1 |
| DB16327 | Sepofarsen | 2 / 3 | Recruiting | 1 |
| DB13932 | Voretigene neparvovec | 3 | Active Not Recruiting | 1 |