Cystinosis, Nephropathic
Also known as: Nephropathic Cystinosis / Infantile nephropathic cystinosis (disorder) / Fanconi Bickel Syndrome / Glycogenosis with glucoaminophosphaturia (disorder) / Cystinosis / Cystinosis (disorder)
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB00847 | Cysteamine | A cystine depleting agent used to treat the effects of cystinosis. |
| Drug | Drug Name | Target | Type |
|---|---|---|---|
| DB00847 | Cysteamine | Neuropeptide Y receptor type 2 | target |
| DB00847 | Cysteamine | Cystine | target |
| DB00847 | Cysteamine | Myeloperoxidase | enzyme |
| DB00847 | Cysteamine | Serum albumin | carrier |
| Drug | Drug Name | Phase | Status | Count |
|---|---|---|---|---|
| DB00847 | Cysteamine | Not Available | Completed | 1 |
| DB00847 | Cysteamine | Not Available | Enrolling by Invitation | 1 |