Transfusion-dependent Thalassemia
Also known as: Transfusion Dependent Thalassemia / Transfusion dependent thalassaemia / Thalassemia / (Thalassaemia (& Mediterranean anaemia)) or (leptocytosis, hereditary) / (Thalassaemia) or (pyruvate kinase deficiency) / Thalassaemia / Thalassemia syndrome (disorder) / Mediterranean anemia (with other hemoglobinopathy) / Thalassaemia NOS / Thalassaemias / Thalassaemic disorders / Thalassemias / Thalassemia (disorder) / (Mediterranean anaemia) or (thalassaemia NOS) / Thalassemia NOS (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB01041 | Thalidomide | 1 | Completed | 1 |
DB01609 | Deferasirox | 2 | Completed | 1 |
DB01005 | Hydroxyurea | 4 | Recruiting | 1 |
DB01041 | Thalidomide | 4 | Recruiting | 1 |
DB03904 | Urea | 4 | Recruiting | 1 |