ALA Dehydratase Deficient Porphyria (ADP)

Also known as: Delta-aminolevulinic acid dehydratase deficient porphyria / Porphyria acute / Porphyria, Acute Intermittent / Acute intermittent porphyria / Acute intermittent porphyria (disorder) [Ambiguous] / Acute intermittent porphyria (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB15066Givosiran3Completed1