Hereditary transthyretin-mediated amyloidosis
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB14582 | Patisiran | A transthyretin-directed small interfering RNA used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis. |
| DB16699 | Vutrisiran | A transthyretin-directed small interfering RNA used to treat polyneuropathy associated with hereditary transthyretin-mediated amyloidosis. |
| Drug | Drug Name | Target | Type |
|---|---|---|---|
| DB14582 | Patisiran | Transthyretin mRNA | target |
| DB14582 | Patisiran | Serum albumin | carrier |
| DB14582 | Patisiran | alpha1-acid glycoprotein | carrier |
| DB16699 | Vutrisiran | Transthyretin mRNA | target |
| DB16699 | Vutrisiran | Serum albumin | carrier |
| Drug | Drug Name | Phase | Status | Count |
|---|