Adult Spinal Muscular Atrophy
Also known as: Spinal muscular atrophy adult onset / Adult spinal muscular atrophy (disorder) / Myelopathic Muscular Atrophy
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB13161 | Nusinersen | Not Available | Completed | 1 |