Adult Spinal Muscular Atrophy

Also known as: Spinal muscular atrophy adult onset / Adult spinal muscular atrophy (disorder) / Myelopathic Muscular Atrophy

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB13161NusinersenNot AvailableCompleted1