Lysosomal Diseases Recruiting Phase 1 / 2 Trials for Prednisone (DB00635)

IndicationStatusPhase
DBCOND0119875 (Lysosomal Diseases)Recruiting1 / 2
clinicaltrials.gov IdentifierTitlePurposeDrugs
NCT03952637A Phase 1/2 Study of Intravenous Gene Transfer With an AAV9 Vector Expressing Human <=-Galactosidase in Type I and Type II GM1 GangliosidosisTreatment