Severe Combined Immunodeficiency Syndrome caused by Adenosine Deaminase Deficiency

Also known as: Severe Combined Immunodeficiency Due to ADA Deficiency / Severe Combined Immunodeficiency Due to Adenosine Deaminase Deficiency / Adenosine Deaminase Deficiency Severe Combined Immunodeficiencies (SCID) / Adenosine Deaminase Severe Combined Immune Deficiency / Adenosine DeAminase Severe Combined ImmunoDeficiency (ADA-SCID) / Adenosine Deaminase Deficiency - SCID / SCID due to absent lymphoid stem cells (disorder)

Drug	Drug Name	Drug Description
DB14712	Elapegademase	A recombinant adenosine deaminase used to treat adenosine deaminase severe combined immune deficiency.

Drug	Drug Name	Target	Type
DB14712	Elapegademase	Adenosine	target

Drug	Drug Name	Phase	Status	Count
DB01008	Busulfan	1 / 2	Completed	2
DB17594	Strimvelis	Not Available	Completed	1