Porphyrias, Hepatic

Name
Porphyrias, Hepatic
Accession Number
DBCAT005552
Description

Not Available

Drugs
DrugDrug Description
GivosiranA 5-aminolevulinic acid synthase-directed small interfering RNA (siRNA) used in the prophylaxis of acute hepatic porphyria.
Drugs & Drug Targets
DrugTargetType
GivosiranALAS1 mRNAtarget