Aminolevulinate Synthase 1-Directed Small Interfering RNAs
- Name
- Aminolevulinate Synthase 1-Directed Small Interfering RNAs
- Accession Number
- DBCAT005670
- Description
RNA interference therapies that inhibit aminolevulinate synthase-1 expression.
- Drugs
Drug Drug Description Givosiran A 5-aminolevulinic acid synthase-directed small interfering RNA (siRNA) used in the prophylaxis of acute hepatic porphyria. - Drugs & Drug Targets
Drug Target Type Givosiran ALAS1 mRNA target