Non-Replicating Recombinant, Self-Complementary Adeno-Associated Virus Serotype 9 Containing the Human CLN3 Gene

Name
Non-Replicating Recombinant, Self-Complementary Adeno-Associated Virus Serotype 9 Containing the Human CLN3 Gene
Accession Number
DBCAT005765
Description

Not Available

Drugs
DrugDrug Description
AT-GTX-502AT-GTX-502 is an experimental, one-time gene therapy that uses AAV9 to deliver a functional copy of CLN3.
Drugs & Drug Targets
DrugTargetType