Alkaptonuria
Also known as: Ochronosis / Other disorders of tyrosine metabolism / Ochronosis due to homogentisate 1,2-dioxygenase deficiency (disorder) / Black urine disease / Homogentisate 1,2-dioxygenase deficiency (disorder) / Exogenous ochronosis (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB00348 | Nitisinone | 2 | Completed | 2 |
DB00348 | Nitisinone | 2 / 3 | Completed | 1 |
DB00348 | Nitisinone | 3 | Unknown Status | 1 |