Congenital Thrombotic Thrombocytopenic Purpura

Also known as: Upshaw-Schulman syndrome (disorder)

DrugDrug NameDrug Description
DB15164Apadamtase alfaA recombinant human ADAMTS13 for enzyme replacement therapy in patients with congenital thrombotic thrombocytopenic purpura.
DrugDrug NameTargetType
DB15164Apadamtase alfavon Willebrand factortarget
DrugDrug NamePhaseStatusCount