Mucopolysaccharidosis Type IH
Also known as: Hurler's syndrome / Dysostosis multiplex (disorder) / Hurler Syndrome / MPS I H / Mucopolysaccharidosis, MPS-I-H (disorder) / Hurler's disease
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB00090 | Laronidase | Not Available | Terminated | 1 |