Familial Amyloid Polyneuropathy (FAP)

Also known as: Familial Amyloid Polyneuropathies / Familial Amyloid Polyneuropathy / Hereditary neuropathic amyloidosis / Neuropathic heredofamilial amyloidosis / Amyloid Neuropathies, Familial / Familial amyloid polyneuropathy (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00861Diflunisal2 / 3Completed1
DB05352Fx-1006A2 / 3Completed2
DB14713Inotersen2 / 3Completed1
DB14713Inotersen3Completed1
DB14582Patisiran3Completed1
DB14582PatisiranNot AvailableNo Longer Available1