Danon Disease

Also known as: Lysosome-associated membrane protein 2 (LAMP-2) Deficiency / Lysosome-associated membrane protein 2 [LAMP2] deficiency / Glycogen Storage Disease Type IIb / Glycogen storage disease due to lysosomal associated membrane protein 2 deficiency (disorder) / Glycogen storage disease, type II (disorder) / Pompe disease / Glycogen storage disease type II / Type II glycogen storage disease / Pompe's disease

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB17647RP-A5011Active Not Recruiting1