Hereditary Transthyretin Amyloidosis

DrugDrug NameDrug Description
DB14713InotersenAn antisense oligonucleotide used to treat polyneuropathy of hereditary transthyretin-mediated amyloidosis.
DrugDrug NameTargetType
DB14713InotersenTransthyretin mRNAtarget
DrugDrug NamePhaseStatusCount