GM1 Gangliosidosis, Type 2

Also known as: Gangliosidosis, Generalized GM1, Type 2 / Juvenile GM>1< gangliosidosis (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB18581PBGM011 / 2Active Not Recruiting1