Delta-aminolevulinic acid dehydratase deficient porphyria

Also known as: ALA Dehydratase Deficient Porphyria (ADP) / Porphyria acute / Porphyria, Acute Intermittent / Acute intermittent porphyria / Acute intermittent porphyria (disorder) [Ambiguous] / Acute intermittent porphyria (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB15066Givosiran3Completed1