Sepofarsen
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This drug entry is a stub and has not been fully annotated. It is scheduled to be annotated soon.
Identification
- Generic Name
- Sepofarsen
- DrugBank Accession Number
- DB16327
- Background
Sepofarsen is under investigation in clinical trial NCT03913143 (A Study to Evaluate Efficacy, Safety, Tolerability and Exposure After a Repeat-dose of Sepofarsen (QR-110) in LCA10 (ILLUMINATE)).
- Type
- Biotech
- Groups
- Investigational
- Biologic Classification
- Gene Therapies
Antisense oligonucleotides - Synonyms
- Sepofarsen
- External IDs
- QR 110
- QR-110
- QR110
Pharmacology
- Indication
Not Available
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- Pharmacodynamics
Not Available
- Mechanism of action
- Not Available
- Absorption
Not Available
- Volume of distribution
Not Available
- Protein binding
Not Available
- Metabolism
- Not Available
- Route of elimination
Not Available
- Half-life
Not Available
- Clearance
Not Available
- Adverse Effects
- Improve decision support & research outcomesWith structured adverse effects data, including: blackbox warnings, adverse reactions, warning & precautions, & incidence rates. View sample adverse effects data in our new Data Library!Improve decision support & research outcomes with our structured adverse effects data.
- Toxicity
Not Available
- Pathways
- Not Available
- Pharmacogenomic Effects/ADRs
- Not Available
Interactions
- Drug Interactions
- This information should not be interpreted without the help of a healthcare provider. If you believe you are experiencing an interaction, contact a healthcare provider immediately. The absence of an interaction does not necessarily mean no interactions exist.Not Available
- Food Interactions
- Not Available
Categories
- ATC Codes
- S01XA29 — Sepofarsen
- Drug Categories
- Classification
- Not classified
- Affected organisms
- Not Available
Chemical Identifiers
- UNII
- 7CAZ46X8EL
- CAS number
- 2227173-68-2
References
- General References
- Not Available
- External Links
- Not Available
Clinical Trials
- Clinical Trials
Phase Status Purpose Conditions Count 2, 3 Active Not Recruiting Treatment Blindness / Eye Diseases / Eye Diseases, Hereditary / Eye disorders congenital / Leber Congenital Amaurosis (LCA) / Leber Congenital Amaurosis 10 / Neurologic Manifestations / Retinal Diseases / Sensation Disorders / Vision Disorders 1 2, 3 Recruiting Treatment Blindness / Eye Diseases / Eye disorders congenital / Leber Congenital Amaurosis (LCA) / Leber Congenital Amaurosis 10 / Neurologic Manifestations / Retinal Degenerations / Retinal Diseases / Retinal Dystrophies / Sensation Disorders / Vision Disorders 1 1, 2 Completed Treatment Leber Congenital Amaurosis (LCA) 1 1, 2 Terminated Treatment Blindness / Eye Diseases / Eye Diseases, Hereditary / Eye disorders congenital / Leber Congenital Amaurosis (LCA) / Leber Congenital Amaurosis 10 / Neurologic Manifestations / Retinal Diseases / Sensation Disorders / Vision Disorders 1
Pharmacoeconomics
- Manufacturers
- Not Available
- Packagers
- Not Available
- Dosage Forms
- Not Available
- Prices
- Not Available
- Patents
- Not Available
Properties
- State
- Not Available
- Experimental Properties
- Not Available
Drug created at December 15, 2020 20:02 / Updated at September 26, 2023 22:59