Alpha Mannosidosis

Also known as: Alpha-D-Mannosidosis / Alpha-Mannosidase Deficiency / Alpha-Mannosidosis / Deficiency of alpha-mannosidase (disorder) / Mannosidosis (disorder) / Defects in glycoprotein degradation / Mannosidase Deficiency Diseases

DrugDrug NameDrug Description
DB12374Velmanase alfaA recombinant human lysosomal alpha-mannosidase used to treat non-neurological symptoms of mild to moderate alpha-mannosidosis.
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB12374Velmanase alfa1Completed1
DB00087Alemtuzumab2Completed1
DB00087Alemtuzumab2Terminated1
DB01008Busulfan2Completed1
DB01008Busulfan2Terminated1
DB00531Cyclophosphamide2Completed1
DB00531Cyclophosphamide2Terminated1
DB00091Cyclosporine2Completed1
DB00688Mycophenolate mofetil2Completed1
DB12374Velmanase alfa2Completed2
DB12374Velmanase alfa2Unknown Status1
DB12374Velmanase alfa3Completed4
DB12374Velmanase alfa3Withdrawn1
DB12374Velmanase alfaNot AvailableAvailable1
DB12374Velmanase alfaNot AvailableNot Yet Recruiting1