Congenital Pure Red Cell Aplasia

Also known as: Constitutional (pure) red blood cell aplasia / Anemia, Diamond-Blackfan / Chronic constitutional pure red cell aplasia (disorder) / Diamond-Blackfan anemia / Diamond-Blackfan anaemia / Aase syndrome / Aase syndrome (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00098Antithymocyte immunoglobulin (rabbit)2Recruiting1
DB00531Cyclophosphamide2Active Not Recruiting1
DB01073Fludarabine2Active Not Recruiting1
DB01073Fludarabine2Recruiting1
DB16620Methopterin2Recruiting1
DB00563Methotrexate2Recruiting1
DB00864Tacrolimus2Recruiting1
DB11678Treosulfan2Recruiting1