Congenital Pure Red Cell Aplasia
Also known as: Constitutional (pure) red blood cell aplasia / Anemia, Diamond-Blackfan / Chronic constitutional pure red cell aplasia (disorder) / Diamond-Blackfan anemia / Diamond-Blackfan anaemia / Aase syndrome / Aase syndrome (disorder)
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB00098 | Antithymocyte immunoglobulin (rabbit) | 2 | Recruiting | 1 |
DB00531 | Cyclophosphamide | 2 | Active Not Recruiting | 1 |
DB01073 | Fludarabine | 2 | Active Not Recruiting | 1 |
DB01073 | Fludarabine | 2 | Recruiting | 1 |
DB16620 | Methopterin | 2 | Recruiting | 1 |
DB00563 | Methotrexate | 2 | Recruiting | 1 |
DB00864 | Tacrolimus | 2 | Recruiting | 1 |
DB11678 | Treosulfan | 2 | Recruiting | 1 |