Bardet Biedl Syndrome (BBS)
Also known as: Bardet-Biedl Syndrome / Bardet Biedl Syndrome / Laurence-Moon-Bardet-Biedl syndrome / Bardet-Biedl Syndrome (BBS) / Bardet-Biedl syndrome (disorder) / Laurence-Moon syndrome / Laurence-Moon syndrome (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB11700 | Setmelanotide | Setmelanotide is indicated to treat obesity caused by genetic POMC, PCSK1, or LEPR deficiencies or Bardet-Biedl syndrome. |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB11700 | Setmelanotide | Melanocortin receptor 4 | target |
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB00331 | Metformin | 2 | Withdrawn | 1 |
DB11700 | Setmelanotide | 3 | Completed | 3 |
DB11700 | Setmelanotide | Not Available | Approved for Marketing | 1 |