Mild, moderate Gaucher Disease, Type 1
| Drug | Drug Name | Drug Description |
|---|---|---|
| DB00419 | Miglustat | A glucosylceramide synthase inhibitor used for the management of mild to moderate type I Gaucher disease for patients who are not candidates for whole enzyme replacement. |
| Drug | Drug Name | Target | Type |
|---|---|---|---|
| DB00419 | Miglustat | Ceramide glucosyltransferase | target |
| Drug | Drug Name | Phase | Status | Count |
|---|