Pyruvate kinase deficiency anaemia
Also known as: Pyruvate Kinase Deficiency Anemia / Anemia due to pyruvate kinase deficiency / HNSHA due to pyruvate kinase deficiency (disorder)
Drug | Drug Name | Drug Description |
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DB16236 | Mitapivat | A pyruvate kinase activator used to treat hemolytic anemia in adults with pyruvate kinase (PK) deficiency. |
Drug | Drug Name | Phase | Status | Count |
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