GNE Myopathy
Also known as: Hereditary Inclusion Body Myopathy / Hereditary Inclusion Body Myopathy (HIBM) / Distal Myopathy, Nonaka Type / Nonaka Myopathy / Nonaka Disease / Inclusion body myopathy 2 (disorder)
Drug | Drug Name | Drug Description |
---|
Drug | Drug Name | Target | Type |
---|
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB11797 | Aceneuramic acid | 1 | Completed | 1 |
DB12536 | N-acetylmannosamine | 1 | Completed | 1 |
DB11797 | Aceneuramic acid | 2 | Terminated | 1 |
DB12536 | N-acetylmannosamine | 2 | Active Not Recruiting | 1 |
DB12536 | N-acetylmannosamine | 2 | Completed | 1 |
DB11797 | Aceneuramic acid | 3 | Completed | 2 |
DB11797 | Aceneuramic acid | 3 | Terminated | 1 |