Distal Myopathy With Rimmed Vacuoles (DMRV)
Also known as: Distal Myopathy With Rimmed Vacuoles / GNE myopathy / Inclusion body myopathy 2 (disorder) / Hereditary inclusion body myopathy
Drug | Drug Name | Drug Description |
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Drug | Drug Name | Target | Type |
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Drug | Drug Name | Phase | Status | Count |
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DB11797 | Aceneuramic acid | 2 | Terminated | 1 |
DB11797 | Aceneuramic acid | 3 | Completed | 2 |
DB11797 | Aceneuramic acid | 3 | Terminated | 1 |