Mucopolysaccharidosis IIIB

Also known as: MPS 3 B / MPS IIIB (Sanfilippo Syndrome) / Sanfilippo B / Mucopolysaccharidosis III-B / Sanfilippo Syndrome B / Mucopolysaccharidosis Type 3 B / Sanfilippo Syndrome Type B / MPS III B / Mucopolysaccharidosis III, Type B (MPS IIIB) / Mucopolysaccharidosis Type IIIB / MPS IIIB (Sanfilippo B Syndrome) / Sanfilippo mucopolysaccharidoses / Mucopolysaccharidosis, MPS-III-B (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB11105Benzalkonium1 / 2Completed1
DB15267Lesinidase alfa1 / 2Completed1
DB15267Lesinidase alfa1 / 2Terminated1
DB17657Tralesinidase alfa1 / 2Completed1
DB17657Tralesinidase alfa2Active Not Recruiting1
DB17657Tralesinidase alfa4Enrolling by Invitation1