Cystinosis

Also known as: Cystinosis (disorder)

DrugDrug NameDrug Description
DB00847CysteamineA cystine depleting agent used to treat the effects of cystinosis.
DrugDrug NamePhaseStatusCount
DB00847Cysteamine1Completed1
DB14480Acetylcysteine amide1 / 2Recruiting1
DB00531Cyclophosphamide1 / 2Recruiting1
DB00847Cysteamine1 / 2Completed1
DB00847Cysteamine1 / 2Recruiting1
DB01073Fludarabine1 / 2Recruiting1
DB01042Melphalan1 / 2Recruiting1
DB00073Rituximab1 / 2Recruiting1
DB00052Somatotropin1 / 2Withdrawn1
DB00847Cysteamine2Completed1
DB15080ELX-022Terminated1
DB00847Cysteamine3Completed5
DB00151Cysteine4Completed1
DB00847CysteamineNot AvailableCompleted2
DB00847CysteamineNot AvailableRecruiting1