Inborn Errors of Metabolism

Also known as: Inborn error of metabolism / Metabolism, Inborn Errors / Inborn error of metabolism NOS / Metabolic hereditary disorder

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB00087Alemtuzumab1Completed1
DB01073Fludarabine1Completed1
DB01005Hydroxyurea1Completed1
DB01042Melphalan1Completed1
DB04572Thiotepa1Completed1
DB00087Alemtuzumab2Completed1
DB09312Antilymphocyte immunoglobulin (horse)2Completed1
DB01008Busulfan2Active Not Recruiting1
DB01008Busulfan2Completed1
DB06775Carglumic acid2Withdrawn1
DB00531Cyclophosphamide2Completed1
DB01073Fludarabine2Completed1
DB01042Melphalan2Completed1
DB04951Pirfenidone2Completed1
DB04572Thiotepa2Completed1
DB11678Treosulfan2Active Not Recruiting1
DB06775Carglumic acid2 / 3Active Not Recruiting1
DB04974RimiducidNot AvailableNo Longer Available1