Neuronal Ceroid Lipofuscinosis

Also known as: Neuronal Ceroid-Lipofuscinoses / Batten Disease / Batten's Disease / Neuronal ceroid lipofuscinosis (disorder) / Neuronal ceroid lipofuscinosis NOS / Juvenile Neuronal Ceroid Lipofuscinosis / Batten's syndrome / Juvenile neuronal ceroid lipofuscinosis (disorder) / Vogt-Spielmeyer disease / Kufs disease / Adult neuronal ceroid lipofuscinosis / Adult neuronal ceroid lipofuscinosis (disorder) / Late-Infantile Neuronal Ceroid Lipofuscinosis / Late-infantile neuronal ceroid lipofuscinosis (disorder)

DrugDrug NameDrug Description
DrugDrug NameTargetType
DrugDrug NamePhaseStatusCount
DB13173Cerliponase alfa1 / 2Completed2
DB00419Miglustat1 / 2Active Not Recruiting1
DB13173Cerliponase alfa2Completed1
DB01008Busulfan2 / 3Completed1
DB00531Cyclophosphamide2 / 3Completed1