Metachromatic Leukodystrophy (MLD)
Also known as: Leukodystrophy, Metachromatic / Metachromatic Leukodystrophy / MLD / Other sphingolipidosis / Metachromatic leukodystrophy, juvenile type (disorder) / Metachromatic leucodystrophy (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB17538 | Atidarsagene autotemcel | A gene therapy comprising autologous CD34+ enriched stem cells encoding the human arylsulfatase A (ARSA) gene used to treat metachromatic leukodystrophy (MLD). |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB17538 | Atidarsagene autotemcel | Human Arylsulfatase A mRNA | target |
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB17671 | Recombinant human arylsulfatase A | 1 / 2 | Active Not Recruiting | 1 |
DB17671 | Recombinant human arylsulfatase A | 1 / 2 | Completed | 1 |
DB17644 | TAK-611 | 1 / 2 | Active Not Recruiting | 1 |
DB17644 | TAK-611 | 1 / 2 | Completed | 1 |
DB00087 | Alemtuzumab | 2 | Completed | 2 |
DB01008 | Busulfan | 2 | Completed | 1 |
DB00631 | Clofarabine | 2 | Completed | 1 |
DB06189 | Clofarabine | 2 | Completed | 1 |
DB00531 | Cyclophosphamide | 2 | Completed | 1 |
DB00091 | Cyclosporine | 2 | Completed | 1 |
DB01005 | Hydroxyurea | 2 | Completed | 1 |
DB01042 | Melphalan | 2 | Completed | 1 |
DB00688 | Mycophenolate mofetil | 2 | Completed | 1 |
DB17671 | Recombinant human arylsulfatase A | 2 | Active Not Recruiting | 1 |
DB17644 | TAK-611 | 2 | Active Not Recruiting | 1 |
DB01008 | Busulfan | 2 / 3 | Completed | 1 |
DB00531 | Cyclophosphamide | 2 / 3 | Completed | 1 |
DB04974 | Rimiducid | Not Available | No Longer Available | 1 |
DB00682 | Warfarin | Not Available | Completed | 1 |