Mucopolysaccharidosis IH
Also known as: Hurlers Syndrome / Hurler's Syndrome / Hurler Syndrome / Hurler Syndrome (MPS I) / Dysostosis multiplex (disorder) / MPS I H / Mucopolysaccharidosis, MPS-I-H (disorder) / Hurler's disease / Mucopolysaccharidosis, type I / Mucopolysaccharidosis I / Mucopolysaccharidosis, MPS-I (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB00090 | Laronidase | A form of recombinant human alpha-L-iduronidase used to treat Hurler and Hurler-Scheie forms of mucopolysaccharidosis, a genetic deficiency of alpha-L-iduronidase. |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB00090 | Laronidase | Iduronic acid | target |
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB01281 | Abatacept | 1 | Completed | 1 |
DB00090 | Laronidase | 1 | Completed | 2 |
DB04572 | Thiotepa | 1 / 2 | Completed | 1 |
DB00087 | Alemtuzumab | 2 | Completed | 1 |
DB00087 | Alemtuzumab | 2 | Terminated | 1 |
DB01008 | Busulfan | 2 | Completed | 1 |
DB01008 | Busulfan | 2 | Terminated | 1 |
DB00531 | Cyclophosphamide | 2 | Completed | 1 |
DB00531 | Cyclophosphamide | 2 | Terminated | 1 |
DB00091 | Cyclosporine | 2 | Completed | 1 |
DB00090 | Laronidase | 2 | Completed | 2 |
DB00688 | Mycophenolate mofetil | 2 | Completed | 1 |
DB00090 | Laronidase | 3 | Completed | 3 |
DB11105 | Benzalkonium | 4 | Terminated | 1 |
DB00090 | Laronidase | 4 | Completed | 2 |
DB00090 | Laronidase | 4 | Terminated | 1 |
DB00090 | Laronidase | Not Available | Terminated | 1 |
DB04974 | Rimiducid | Not Available | No Longer Available | 1 |
DB00052 | Somatotropin | Not Available | Withdrawn | 1 |