Pompe's Disease
Also known as: Acid Maltase Deficiency / Pompe Disease / Acid Maltase Deficiency (AMD) / Pompe-Disease / Glycogen Storage Disease Type II / Glycogen Storage Disease Type II (GSD-II) / Glycogen Storage Disease Type II GSD II / Glycogen Storage Disease Type II (GSD II) / Glycogen Storage Disease Type II;Pompe's Disease / Glycogen Storage Disease Type II-Pompe's Disease / Glycogen Storage Disease Type II Pompe Disease / Cardiac glycogenosis (disorder) / Glycogen storage disease, type II (disorder) / Type II glycogen storage disease / Deficiency of alpha-glucosidase (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB01272 | Alglucosidase alfa | An acid alpha- glucosidase (GAA) derivative used as an enzyme replacement therapy for the treatment of Pompe disease in infants and pediatric patients caused by GAA deficiency. |
DB16099 | Avalglucosidase alfa | A lysosomal glycogen-specific enzyme that is used to treat patients one year of age and older with late-onset Pompe disease, or lysosomal acid alpha-glucosidase (GAA) deficiency. |