Mucopolysaccharidosis Type VI
Also known as: Mucopolysaccharidosis Type VI (MPS VI) / Maroteaux-Lamy Syndrome / Mucopolysaccharidosis VI / Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome) / Maroteaux Lamy Syndrome / Maroteaux-Lamy syndrome (disorder) / Deficiency of N-acetylgalactosamine-4-sulfatase (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB01279 | Galsulfase | A recombinant human enzyme used as replacement enzyme therapy for the treatment of of adults and children with Mucopolysaccharidosis VI, a rare genetic disorder caused by a deficiency of a lysosomal enzyme. |
Drug | Drug Name | Target | Type |
---|---|---|---|
DB01279 | Galsulfase | Perilipin-3 | target |
DB01279 | Galsulfase | Dermatan sulfate | target |
Drug | Drug Name | Phase | Status | Count |
---|---|---|---|---|
DB00051 | Adalimumab | 1 / 2 | Active Not Recruiting | 1 |
DB00051 | Adalimumab | 1 / 2 | Completed | 1 |
DB00087 | Alemtuzumab | 2 | Completed | 1 |
DB00087 | Alemtuzumab | 2 | Terminated | 1 |
DB00098 | Antithymocyte immunoglobulin (rabbit) | 2 | Completed | 1 |
DB01008 | Busulfan | 2 | Completed | 2 |
DB01008 | Busulfan | 2 | Terminated | 1 |
DB00531 | Cyclophosphamide | 2 | Completed | 2 |
DB00531 | Cyclophosphamide | 2 | Terminated | 1 |
DB00091 | Cyclosporine | 2 | Completed | 1 |
DB00678 | Losartan | 2 | Active Not Recruiting | 1 |
DB00688 | Mycophenolate mofetil | 2 | Completed | 1 |
DB06609 | Odiparcil | 2 | Completed | 1 |
DB00052 | Somatotropin | 2 / 3 | Terminated | 1 |
DB01279 | Galsulfase | 4 | Completed | 1 |
DB01279 | Galsulfase | Not Available | Terminated | 1 |