Paroxysmal Nocturnal Hemoglobinuria
Also known as: Paroxysmal Nocturnal Haemoglobinuria / Paroxysmal Nocturnal Haemoglobinuria (PNH) / Marchiafava-Micheli Syndrome / PNH - Paroxysmal Nocturnal Hemoglobinuria / Paroxysmal Nocturnal Hemoglobinuria (PNH) / Paroxysmal nocturnal hemoglobinuria [Marchiafava-Micheli] / Paroxysmal nocturnal hemoglobinuria (disorder)
Drug | Drug Name | Drug Description |
---|---|---|
DB15401 | Danicopan | A small molecule complement factor D inhibitor used to treat extravascular hemolysis in patients with paroxysmal nocturnal hemoglobinuria. |
DB01257 | Eculizumab | A recombinant humanized monoclonal antibody used to reduce the risk of hemolysis in paroxysmal nocturnal hemoglobinuria (PNH) and atypical hemolytic uremic syndrome (aHUS). |
DB16200 | Iptacopan | A factor B inhibitor used to treat paroxysmal nocturnal hemoglobinuria. |
DB16694 | Pegcetacoplan | A complement inhibitor indicated in the treatment of adults with paroxysmal nocturnal hemoglobinuria. |
DB11580 | Ravulizumab | A monoclonal antibody used to treat paroxysmal nocturnal hemoglobinuria, atypical hemolytic uremic syndrome, and myasthenia gravis. |